1st Dutch Antisense Therapeutics Symposium

July 9th 2021, Leiden

9:30 - Arrival, Registration and Coffee 

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9:55 - Welcome

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10:00 National keynote lecture

          Annemieke Aartsma-Rus (LUMC): A brief history of exon-skipping therapy development: Developments in the current millennium.

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SESSION 1

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10:45 Roland Brock (Radboudumc) - Peptide-based delivery strategies for antisense oligonucleotides

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11:15 Peter van den Akker (UMCG) - Exon-skipping therapy for dystrophic epidermolysis bullosa

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11:45 Saskia A.J. Lesnik Oberstein (LUMC) - Skipping NOTCH3 exons to prevent protein aggregation in CADASIL patient arteries

12:15 Lunch

SESSION 2

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13:15 Early Career Investigator Presentations* 

          13:15 To be announced after abstract selection

          13:30 To be announced after abstract selection

          13:45 To be announced after abstract selection

          14:00 To be announced after abstract selection

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14:15 International Keynote Lecture:

          Bruno Godinho (Atlanta Therapeutics) - Delivery of stabilized siRNA scaffolds to the central nervous system

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15:00 Marjon Pasmooij (Medicines Evaluation Board) - Antisense to medicine: a regulator’s perspective

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15:30 Poster Pitches*

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15:45 POSTER SESSION with Coffee and Cookies

SESSION 3

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17:00 Mike Schwartz (ProQR Therapeutics) - Results of first-in-human clinical data of intravitreal sepofarsen (QR-110) antisense oligonucleotide in Leber congenital amaurosis type 10

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17:30 Elizabeth Vroom (Duchenne Parent Project Netherlands) - The role of patient organizations in antisense oligonucleotide drug development

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18:00 Awards, closing remarks

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18:10 Drinks and Networking

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19:30 Dinner (not included, pre-registration required)

*Deadline for abstract submission: December 18th 2020

*Announcement of the selected abstracts for presentation and poster pitches: during week 1 2021

Abstract book will be available digitally two weeks before the meeting.

For more info click here

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EVENT SPONSORED BY: