9:45 – 10:15       Registration Open

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10:15 – 10:30     Welcome and official opening

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10:30 – 11:15     International Keynote Lecture 1: Aurélie Goyenvalle, Univ. of Versailles, France

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11:15 – 12:30     Session 1:

                11:15 – 11:45     Invited Speaker 1 (Delivery)

                11:45 – 12:00     Selected Abstract 1

                12:00 – 12: 15    Selected Abstract 2

                12:15 – 12:30     Sponsor pitches

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12:30 – 13:30     Lunch

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13:30 – 15:00 Session 2:

                13:30 – 14:00     Monica Aguila (ProQR Therapeutics)

                                           Title: TBA Topic: New Technologies

                14:00 – 14:15     Selected Abstract 3

                14:15 – 14:30     Selected Abstract 4

                14:30 – 14:45     Selected Abstract 5

                14:45 – 15:00     Selected Abstract 6

       

15:00 – 15:15     Selected Poster Pitches Session 1

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15:15 – 16:30     Poster Session 1 with coffee and tea

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16:30 – 18:00     Session 3:

                16:30 – 17:00     Erik de Vrieze (Radboudumc)

                                           Title: TBA Topic: Preclinical development of antisense therapies for ear-related disorders

                17:00 – 17:15     Selected Abstract 7

                17:15 – 17:30     Selected Abstract 8

                17:30 – 17:45     Selected Abstract 9

                17:45 – 18:10     Virginia Arechavala-Gomeza (Biocruces Bizkaia Health Research Institute, Spain)

                                           Title: TBA Topic: The importance of networking

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18:10 – 18:15 Closing of day 1

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19:30     Networking dinner and pubquiz (not incl. in the registration costs)

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9:00 – 9:45          International Keynote Lecture 2: Timothy Yu, Boston Children’s Hospital, USA

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9:45 – 11:00        Session 4: Dutch Center for RNA Therapeutics (DCRT)

                9:45 – 10:05       Marlen Lauffer (LUMC)

                                           Building a framework for the identification and selection of cases for personalized ASO                                                 treatments

                10:05 – 10:25     Ype Elgsma (ErasmusMC)

                                           ASO treatment for Angelman Syndrome: Promises and threats

                10:25 – 10:45     Rob Collin (Radboudumc)

                                           Splicing modulation therapy for inherited retinal diseases: the example of Stargardt                                                       disease

                10:45 – 11:00     Invited Speaker 5 (Regulatory affairs)

 

11:00 – 11:15     Selected Poster Pitches Session 2

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11:15 – 12:30     Poster Session 2 with coffee and tea

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12:30 – 13:30     Lunch

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13:30 – 15:15     Session 5:

                13:30 – 14:00     Nicole Datson (VICO Therapeutics)

                                           VO659, an allele-preferential CAG repeat-targeting ASO with therapeutic potential for 

                                           patients with Huntington’s disease and spinocerebellar ataxia types 1 and 3

                14:00 – 14:30     Invited Speaker 7 (Patient perspective)

                14:30 – 14:45     Selected Abstract 10

                14:45 – 15:00     Selected Abstract 11

                15:00 – 15:15     Selected Abstract 12

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15:15 – 15:25     Award ceremony

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15:25 – 15:35     Closing remarks

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15:35 – 17:00     Networking drinks